A combined therapeutic approach for pyruvate dehydrogenase deficiency using self-complementary adeno-associated virus serotype-specific vectors and dichloroacetate

Zongchao Han, Kristen Berendzen, Li Zhong, Ira Surolia, Nitin Chouthai, Weihong Zhao, Njeri Maina, Arun Srivastava, Peter W. Stacpoole

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